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Des doses de la thérapie génique pour la myopathie de Duchenne développée par Généthon, le laboratoire de l'AFM-Téléthon
News
19/11/2024

Genethon Presents Promising Results for Gene Therapy in DMD

Genethon, the pioneering gene therapy research laboratory created by AFM-Telethon, today presented positive results from the Phase 1/2 dose escalation part of the trial evaluating its gene therapy, GNT0004, for Duchenne muscular dystrophy (DMD) at the ASGCT Breakthroughs in Muscular Dystrophy conference, Nov. 19 - 20, 2024, in Chicago, IL. Based on these results, Genethon plans to launch a pivotal trial in Europe and the United States in 2025. 

Journée Internationale de sensibilisation aux LGMD
News
30/09/2024

September 30: International LGMD Awareness Day

The 10th International Limb-Girdle Muscular Dystrophy (LGMD) Awareness Day takes place on September 30. Organized by the LGMD Awareness Foundation, the day's mission is to draw attention to this group of rare neuromuscular diseases and their impact on the lives of affected children and adults in all regions of the world. 

Mika, parrain du Téléthon 2024
Telethon
20/09/2024

Telethon 2024: Mika is the new patron !

Alongside the hosts of France Televisions and surrounded by numerous artists, Mika will use all his talent, sensitivity and energy to support families in their fight against rare diseases. Discover his message !

Le 21 septembre, c'est la journée mondiale des Myosites
News
20/09/2024

World Myositis Day on September 21

September 21, 2024 marks the 2nd World Myositis Day. At last year's World Myositis Congress in Berlin, international associations fighting inflammatory myopathies decided to dedicate the day to raising public awareness and mobilizing resources around these rare diseases. This worldwide initiative aims to better understand and treat myositis by uniting efforts on a global scale.

Logo de la journée mondiale sensibilisation aux dystrophies myotoniques
News
13/09/2024

September 15: World Myotonic Dystrophy Awareness Day

September 15, 2024 marks the 4th International Myotonic Dystrophies Awareness Day. This event, supported by over 60 organizations worldwide, aims to raise awareness among the general public, healthcare professionals and political decision-makers of the need to improve diagnosis, care and support for patients, and to speed up the development of medicines. The AFM-Telethon, which brings together French patients affected by these diseases, is committed to speeding up research. This new edition focuses on two specific areas in particular: raising awareness and educating clinical care teams, and preparing participants for clinical trials.

Sacha traité par thérapie génique dans le cadre de l'essai Généthon
News
06/09/2024

World Duchenne Awareness Day: Genethon at the forefront of the fight against Duchenne muscular dystrophy

World Duchenne Muscular Dystrophy Day provides an opportunity to note the acceleration in the development of innovative therapies for this neuromuscular disease, which is the most common in children. Gene therapy is one of the most promising avenues. Genethon, the AFM-Telethon laboratory, is currently developing a drug candidate which has demonstrated its efficacy in the first patients to be treated. Discover our video of patient testimonials ! 

Hélène atteinte d'une myopathie FSH
Event
20/06/2024

World FSHD Day: Advancing Research

On June 20, World FSHD Day reminds us of the importance of raising awareness and supporting research into facioscapulohumeral muscular dystrophy. Committed to the fight against FSHD, the AFM-Téléthon is making available a series of publications to enlight the advances in research by it, but also by many other neuromuscular diseases. 

bénévole tenant des ballons
Telethon
17/05/2024

Telethon 2024: Join the Cause on November 29 and 30!

While it is customary for the heart of solidarity to beat for the Telethon on the first weekend in December, this year, exceptionally, the Telethon will be held on November 29 and 30, to make way for the ceremony to reopen the Cathedral of Notre-Dame de Paris.
 

Carte de voeux 2024 avec les 4 ambassadeurs du téléthon 2023
AFM-Telethon
02/01/2024

Happy new year!


The AFM-Téléthon sends you its best wishes for the New Year and hopes that 2024 will be full of scientific breakthroughs, small and large joys, and shared victories!

Plateau du téléthon 2023 avec 100 chercheurs
Telethon
19/12/2023

Telethon 2023 : €80,671,222: Thanks to you! 

The Telethon 2023 ended on a high of €80,671,222, which shows the confidence and exceptional mobilization of donors and volunteers for this year's event, rich in victories against disease and promises for all those waiting for the diagnosis and treatment that will change their lives. We must not give up.