Un garçon en visite dans le laboratoire Généthon en compagnie d'une chercheuse

AFM-Telethon

Welcome to AFM-Telethon's website

Families and researchers are counting on you !

Latest news

Des doses de la thérapie génique pour la myopathie de Duchenne développée par Généthon, le laboratoire de l'AFM-Téléthon

Genethon Presents Promising Results for Gene Therapy in DMD

Genethon, the pioneering gene therapy research laboratory created by AFM-Telethon, today presented positive results from the Phase 1/2 dose escalation part of the trial evaluating its gene therapy, GNT0004, for Duchenne muscular dystrophy (DMD) at the ASGCT Breakthroughs in Muscular Dystrophy conference, Nov. 19 - 20, 2024, in Chicago, IL. Based on these results, Genethon plans to launch a pivotal trial in Europe and the United States in 2025. 

Mika, parrain du Téléthon 2024

Telethon 2024: Mika is the new patron !

Alongside the hosts of France Televisions and surrounded by numerous artists, Mika will use all his talent, sensitivity and energy to support families in their fight against rare diseases. Discover his message !

Sacha traité par thérapie génique dans le cadre de l'essai Généthon

World Duchenne Awareness Day: Genethon at the forefront of the fight against Duchenne muscular dystrophy

World Duchenne Muscular Dystrophy Day provides an opportunity to note the acceleration in the development of innovative therapies for this neuromuscular disease, which is the most common in children. Gene therapy is one of the most promising avenues. Genethon, the AFM-Telethon laboratory, is currently developing a drug candidate which has demonstrated its efficacy in the first patients to be treated. Discover our video of patient testimonials ! 

Our fight to cure

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60 years of fight against diseases

The French Muscular Dystrophy Association (AFM-Téléthon) is composed of patients and their families who are affected by genetic, rare and progressive diseases. Discover 60 years of fight.

Join the Telethon for french people abroad

You live abroad and want to be part of the great Telethon adventure? Join us!