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While the first gene therapy drugs are obtaining marketing authorization and being made available to patients, the challenge of industrializing their production is a crucial one.

Peeling an apple. Lifting your arms. Walking. Smiling. Breathing. These routine actions use muscles and we accomplish them without thinking. But with neuromuscular diseases, the muscles are attacked and movement is prevented. In order to better treat them, AFM-Telethon wants to make myology a separate discipline. 

Participation in the Telethon or support for our therapeutic and social innovation projects, your company can get involved in various ways. Find out how to become a partner/sponsor of AFM-Telethon.

The French Telethon also takes place abroad. French expatriates can join in this 30-hour marathon of celebration and solidarity from all over the world. You live abroad and want to be part of the great Telethon adventure? Join us!  

You can pass on not only your genes It is above all about deep convictions, to last beyond your lifetime.  

Gene, cellular and pharmacogenetic therapy: AFM-Telethon uses donations to develop new therapies for the most frequent rare diseases.   

AFM-Telethon puts the power of patients at the core of its international activities, with the aim of strengthening the place of French neuromuscular patients in Europe and in the world. 

Innovative therapies for rare diseases are being developed internationally. Base on this observation, AFM-Telethon encourages worldwide collaboration between the most competent teams.

Myobase is a document portal dedicated to neuromuscular diseases and motor disabilities, published by the documentation department at the French Muscular Dystrophy Association. It gives access to over 60,000 documents. 

Thanks to your donations, research is moving forwards, the first treatments have arrived and care and support for people affected by rare diseases has improved. Your donations drive the victories of AFM-Telethon!  

AFM-Telethon is battling on all fronts, from access to diagnosis and appropriate treatment to close support, giving priority to the search for innovative solutions and a response to the needs of patients. 

Encouraging innovation, creating pathways between academic research and private research, supporting those involved in developing the drug: the AFM-Telethon is investing to speed up the arrival of innovative biotherapies. 

To accelerate the development of innovative treatments for rare diseases, the AFM-Telethon has created its own laboratories. Devoted to gene therapy of rare diseases (Genethon), to stem cells (I-Stem) and to myology (Institute of myology), they are now international leaders in their field. Located within the Institute for rare disease biotherapies, the Association’s three laboratories play a major role in the medical revolution.   

Innovation in scientifical, medical, social and technological fields, AFM-Telethon is a pioneer in the research and support to improve patients’ lives. Three missions are at the heart of its action: Cure, Care, Communicate.

The French Muscular Dystrophy Association (AFM-Telethon) is an association of activists, patients and parents of patients, affected by rare, progressive and significantly disabling genetic diseases, known as genetic neuromuscular diseases. It was created out of a conviction and a desire, to cure diseases that were long considered to be incurable. AFM-Telethon is also the Telethon, a fundraising event which brought rare diseases out of scientific and medical obscurity and triggered a three-fold revolution: genetic, social and medical.